RP Cure Tracker

The pipeline

77 active treatment trials, grouped by how they work and how far along they are. Phase 3 is the last step before a company can apply for approval.

Gene therapy

Early Phase 1 / Phase 1 9

Phase 2 18

Phase 3 6

Drug / neuroprotection

Early Phase 1 / Phase 1 6

Phase 2 7

Phase 3 4

Phase 4 1

Cell therapy

Early Phase 1 / Phase 1 2

Phase 2 4

Phase 3 1

Optogenetics

Early Phase 1 / Phase 1 2

  • ZM-02-L Augelux Therapeutics, any gene, recruiting
  • RTx-015 Ray Therapeutics, Inc., any gene

Phase 2 4

Phase 3 1

  • RTx-015 Ray Therapeutics, Inc., any gene, recruiting

RNA / antisense

Early Phase 1 / Phase 1 1

Phase 2 4

Phase 3 2

Gene editing

Early Phase 1 / Phase 1 1

  • ZVS203e Peking University Third Hospital, RHO, recruiting

Phase 2 2

  • ACDN-01 Ascidian Therapeutics, Inc, recruiting
  • ZVS203e Chigenovo Co., Ltd, RHO, recruiting

Supplement / diet

Early Phase 1 / Phase 1 1

  • DF-003 Shanghai Yao Yuan Biotechnology Ltd. (also known as Drug Farm), recruiting

Phase 2 1

Where active trials have sites