Trials / NCT02714816
Natural History Study of Patients With Leber Congenital Amaurosis Associated With Mutations in RPE65
Completed Observational Natural history / observational
- Sponsor
- MeiraGTx UK II Ltd
- Treatment
- Not listed
- Gene
- RPE65
- Conditions
- Leber Congenital Amaurosis
- Ages
- 3 Years to no upper limit
- Enrollment
- 37 participants
- Started
- 2016-04
- Main results expected
- 2023-07-22
- Results posted
- Not yet
- Record last updated
- 2026-09-21
What the study is testing
MGT005 is a natural history study to collect longitudinal prospective data from patients with Leber Congenital Amaurosis associated with defects in RPE65.
Where it runs
United Kingdom (1)
- Moorfields Eye Hospital, London
United States (1)
- Kellogg Eye Center, Ann Arbor, Michigan